Our research summaries provide insights into the latest scientific...
Fabry Disease Patient with Heart Failure Receives Transplant
New GLA Mutations May be Treated with Galafold
Fabry Disease Coexists with Thin Basement Membrane Nephropathy
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Early Intervention for Rare Conditions
Fabry Gene Therapy Maintains Kidney Function
Gene Therapy Exempt from GST, Tax Cuts on Cancer and Rare Disease Medicines Expected
Glafabra's Game-Changing Gene Therapy for Enzyme Deficiencies Expands Horizons
