Weekly Spotlight - 19.12.24

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Latest News

Managing Stroke Risk in Fabry Patients Through Lifestyle Changes and Medical Interventions

The author shares personal strategies to mitigate the risk of stroke associated with Fabry disease, including regular exercise, a balanced diet, managing stress, and adhering to prescribed medications. These measures help manage symptoms and reduce the likelihood of stroke in individuals with fabry disease.

European Medicines Agency Validates Submission for New Treatment

Chiesi Global Rare Diseases and Protalix BioTherapeutics announced that the European Medicines Agency has validated their variation submission for pegunigalsidase alfa, a potential treatment for Fabry disease. This step brings the drug closer to regulatory approval, offering hope for a new therapeutic option for patients.

Truist Predicts Sangamo Stock Growth Due to Milestone Payments and Disease Treatment Progress

Truist analysts predict an increase in Sangamo Therapeutics' stock value due to potential milestone payments and advancements in treatments for Fabry disease. The positive outlook is driven by the company's progress in gene therapy and its potential to address unmet medical needs.